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tel srt :
tél srt :
Last Update: 2012-04-06
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eliglustat is een krachtige en specifieke remmer van glucosylceramidesynthase en fungeert als substraatreductietherapie (srt) voor gd1.
l’éliglustat est un inhibiteur puissant et spécifique de la glucosylcéramide synthase, et agit comme thérapie de réduction de substrat (trs) pour la mg1.
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