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niemann-picks sygdom, type c, er en meget sjælden, altid progressiv og muligvis dødelig neurodegenererende sygdom, som er karakteriseret ved nedsat intracellulær lipidoverførsel.
niemann-pick type c disease is a very rare, invariably progressive and eventually fatal neurodegenerative disorder characterised by impaired intracellular lipid trafficking.
Last Update: 2017-04-26
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i virkeligheden vil den centraliserede procedure kun omfatte nogle få sygdomme.agenturet i london har udvidet sit arbejdsområde tilstrækkeligt til at sikre finansieringen heraf, men de nationale myndigheder har ikke desto mindre selv beholdt de lægemiddelkategorier, man tjener mest på, det vil sige dem, der vedrører neurodegenererende sygdomme og hjerte-kar-sygdomme.
since 1996, the proportion of new medicinal products launched worldwide by europe has fallen from 55% to 28% – in other words, it has halved – and i am not talking here about turnover but about insufficient investment in research and development.in conclusion, it is important that we do not choose the wrong target or strategy in this debate.
Last Update: 2008-03-04
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